FDA Approval! A New Model for BioPharma... Dr. Sam Blackman, Founder & Head of Research and Development, One Day Biopharmaceuticals

BioTech Nation ... with Dr. Moira Gunn

This week on BioTech Nation, Dr. Sam Blackman, Founder and Head of Research and Development from Day One Biopharmaceuticals, shares the story behind the FDA approval of a groundbreaking drug for the most common childhood brain cancer. Driven by the urgent need for pediatric oncology treatments, Day One's innovative approach led to the development of tovorafenib, targeting BRAF-altered pediatric low-grade gliomas. Through the FireFLY trial, they demonstrated significant efficacy, with 52% of patients experiencing tumor shrinkage and 82% showing benefits. Dr. Blackman emphasizes the importance of hope in drug development and discusses Day One's future plans to expand treatment options for childhood cancer.